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FDA批准Givosiran治疗急性肝卟啉症
2019.11.20
On November 20, 2019, the Food and Drug Administration approved givosiran (GIVLAARI, Alnylam Pharmaceuticals, Inc.) for adults with acute hepatic porphyria (AHP)【FDA批准首例治疗遗传性罕见病的疗法】
Efficacy was evaluated in ENVISION (NCT03338816)...
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